Families, with guidance from doctors, must choose the best treatment option for their baby with SCID. The standard treatment is bone marrow transplant, but some forms of SCID can be treated with gene therapy in clinical trials or enzyme replacement therapy. This video explains how the treatments work so that parents can make an informed decision.
Disease Category:
- Severe Combined Immune Deficiency and Combined Immune Deficiency
Resource Category:
- Stem Cell Therapy
- Treatment
- Gene Therapy
Patient Lifestage:
- Infants and Children
Audience:
- Family member of person with PI
- Medical Professional
- Person with PI
